News Medical2h
Assessment of gene therapy viral vectors in RPE cells
This research evaluates the effects of various gene therapy viral vectors on RPE cells to determine efficacy for therapeutic ...
FierceBiotech15h
Neurogene reports death of Rett patient left in critical condition by high dose of gene therapy
A patient has died after receiving the high dose of Neurogene’s Rett syndro | A patient has died after receiving the high ...
Labroots5d
A New Approach in Usher Syndrome Gene Therapy
Delivering very large genes to cells can pose a serious challenge, so scientists developed a new method. | Genetics And ...
Yahoo Finance4d
Siren Biotechnology Reveals SRN-101 as Lead Asset for High-Grade Gliomas with Both Orphan Drug and Rare Pediatric Disease Designations from the FDA
SRN-101 is a recombinant adeno-associated viral (AAV) vector expressing an engineered cytokine. Last year, Siren ...
OXB to host a free webinar on accelerating development of viral vectors through automated manufacturing and analytical development
OXB to host a free webinar on accelerating development of viral vectors through automated manufacturing and analytical developmentOxford, UK – 20 ...
FiercePharma11d
Thermo Fisher charts 160 layoffs in Massachusetts amid viral vector overhaul
In a bid to streamline viral vector manufacturing, Thermo Fisher is charting another round of layoffs this year—and ...
Harvard Medical School7d
Second Gene Therapy Shows Promise for Syndrome Involving Blindness, Deafness
Harvard Medical School researchers have taken another decisive step in their efforts to develop a gene therapy for people ...
precisionmedicineonline4d
Neurogene Halts Testing High-Dose Rett Syndrome Gene Therapy After Adverse Event
Following this update, the company's stock price dropped more than 30 percent from market close Friday to $23.79 per share Monday morning.
Daily7d
FDA Approves First Gene Therapy for Treatment of AADC deficiency
The U.S. Food and Drug Administration approved Kebilidi (eladocagene exuparvovec-tneq), an adeno-associated virus ...
FierceBiotech8d
Muscular dystrophy gene therapy uses cells to stitch together mRNA strands in mice
Gene therapy for some diseases, including Duchenne muscular dystrophy (DMD), can be tricky because the needed gene is often ...
Business Insider3d
Medera and Singapore’s Cardiovascular Disease National Collaborative Enterprise Launch Asia's First Cardiac Gene Therapy Trial for Heart Failure
SRD-001/2/3 employ an adeno-associated virus (AAV)-based vector system, delivered directly to cardiac ventricular muscle cells via Sardocor’s proprietary intracoronary infusion system. Furthermore, ...