Glycogen storage disease type 1a (von Gierke disease ... The infant was started on dietary treatment with frequent meals, restriciton of glucose and lactose, two meals with uncooked starch ...
"There really is no treatment at all ... Danon disease is a rare X-linked lysosomal glycogen storage disease caused by genetic mutations in the LAMP2 gene. It typically manifests as cardiomyopathy ...
Several chimeric antigen receptor (CAR) T cell therapies are approved for the treatment of various ... potential as a durable therapy for glycogen storage disease type-Ia, correcting both the ...
The "Pompe Disease - Pipeline Insight, 2024" clinical trials has been added to ResearchAndMarkets.com's offering.The report provides comprehensive insights about 15+ companies and 20+ pipeline drugs ...
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