This research evaluates the effects of various gene therapy viral vectors on RPE cells to determine efficacy for therapeutic ...

A patient has died after receiving the high dose of Neurogene’s Rett syndro | A patient has died after receiving the high ...

Delivering very large genes to cells can pose a serious challenge, so scientists developed a new method. | Genetics And ...

OXB to host a free webinar on accelerating development of viral vectors through automated manufacturing and analytical developmentOxford, UK – 20 ...

SRN-101 is a recombinant adeno-associated viral (AAV) vector expressing an engineered cytokine. Last year, Siren ...

Harvard Medical School researchers have taken another decisive step in their efforts to develop a gene therapy for people ...

Following this update, the company's stock price dropped more than 30 percent from market close Friday to $23.79 per share Monday morning.

Ascend Advanced Therapies, which has been on an expansion tear since debuting three years ago, inked a deal with EW ...

Gene therapy for some diseases, including Duchenne muscular dystrophy (DMD), can be tricky because the needed gene is often ...

SRD-001/2/3 employ an adeno-associated virus (AAV)-based vector system, delivered directly to cardiac ventricular muscle cells via Sardocor’s proprietary intracoronary infusion system. Furthermore, ...

The U.S. Food and Drug Administration approved Kebilidi (eladocagene exuparvovec-tneq), an adeno-associated virus ...