The adeno-associated virus vector-based gene therapy is the first FDA-approved gene therapy for treatment of AADC deficiency, ...
Virus. When you hear the word, you probably shudder. But not all viruses are bad or cause disease. Some are even used for ...
Rocket Pharmaceuticals, Inc. (NASDAQ: RCKT), a fully integrated, late-stage biotechnology company advancing a sustainable pipeline of genetic therapies for rare disorders with high unmet need, today ...