News Medical7h
Assessment of gene therapy viral vectors in RPE cells
This research evaluates the effects of various gene therapy viral vectors on RPE cells to determine efficacy for therapeutic ...
OXB to host a free webinar on accelerating development of viral vectors through automated manufacturing and analytical development
OXB to host a free webinar on accelerating development of viral vectors through automated manufacturing and analytical ...
FierceBiotech20h
Neurogene reports death of Rett patient left in critical condition by high dose of gene therapy
A patient has died after receiving the high dose of Neurogene’s Rett syndro | A patient has died after receiving the high ...
FiercePharma8d
Ascend continues to climb with deal that elevates the CDMO’s US footprint
Ascend Advanced Therapies, which has been on an expansion tear since debuting three years ago, inked a deal with EW ...
manilatimes4d
Siren Biotechnology Reveals SRN-101 as Lead Asset for High-Grade Gliomas with Both Orphan Drug and Rare Pediatric Disease Designations from the FDA
Siren Biotechnology's Approach Could Transform the High-Grade Glioma Therapy Landscape "SRN-101 has the potential to address ...
Harvard Medical School7d
Second Gene Therapy Shows Promise for Syndrome Involving Blindness, Deafness
Harvard Medical School researchers have taken another decisive step in their efforts to develop a gene therapy for people ...
Labroots5d
A New Approach in Usher Syndrome Gene Therapy
Delivering very large genes to cells can pose a serious challenge, so scientists developed a new method. | Genetics And ...
Medindia10d
Avirmax Inc. to Present at the ARVO Frontiers in Ocular Gene Therapy Research Conference
Avirmax's Chief Executive and Scientific Officer, Dr. Shengjiang Shawn Liu, Ph.D., will chair the upcoming session of "Acceleration of AAV Gene Therapy for Ocular Diseases: Improving Delivery and ...
FDA Approves First Gene Therapy for Treatment of Aromatic L-amino Acid Decarboxylase Deficiency
The U.S. Food and Drug Administration approved Kebilidi (eladocagene exuparvovec-tneq), an adeno-associated virus vector-based gene therapy indicated for the treatment of adult ...
Neuroscience News4d
Dual-Gene Therapy Shows Promise for Hearing and Vision Loss
Researchers have developed a dual-gene therapy approach to treat Usher syndrome type 1F, a rare condition causing deafness and progressive blindness.