The adeno-associated virus vector-based gene therapy is the first FDA-approved gene therapy for treatment of AADC deficiency, ...

Virus. When you hear the word, you probably shudder. But not all viruses are bad or cause disease. Some are even used for ...

Rocket Pharmaceuticals, Inc. (NASDAQ: RCKT), a fully integrated, late-stage biotechnology company advancing a sustainable pipeline of genetic therapies for rare disorders with high unmet need, today ...

A live virus vaccine contains a live, weakened (attenuated) virus that helps your body develop an immune response without you developing symptoms of the disease it is intended to prevent. Examples ...

Researchers spot new campaign that can turn off antivirus protection Malware uses legitimate Avast Anti-Rootkit driver to ...

The patient died from complications linked to a rare hyperinflammatory syndrome associated with exposure to high doses of the AAV therapy delivery vehicle.

This research evaluates the effects of various gene therapy viral vectors on RPE cells to determine efficacy for therapeutic ...

According to Alnylam’s Tim Mooney, mivelsiran’s endurance is due to stabilizing tweaks the scientists made to the siRNA ...

A patient has died after receiving the high dose of Neurogene’s Rett syndro | A patient has died after receiving the high ...

OXB to host a free webinar on accelerating development of viral vectors through automated manufacturing and analytical ...