Yahoo Finance6d
Pompe Disease Pipeline Insight 2024,with Comprehensive Insights for 15+ Companies and 20+ Pipeline Drugs in the Pompe Disease Pipeline Landscape
MZE001 is currently being evaluated as a potential oral treatment for patients with Pompe disease, as well as other glycogen storage disorders. Currently, the drug is in Phase I stage of its clinical ...
Nature17d
Two New Mutations in the Glucose-6-Phosphatase Gene Cause Glycogen Storage Disease in Hungarian Patients
Glycogen storage disease type 1a (von Gierke disease ... The infant was started on dietary treatment with frequent meals, restriciton of glucose and lactose, two meals with uncooked starch ...