A multinational study led by the LHON Study Group has revealed sustained visual improvements and a favorable safety profile ...

Merck in-licensed a preclinical oral GLP-1 candidate from China's Hansoh Pharma. Astellas doubled down in gene therapy with a ...

Landmark publication in leading ophthalmology research journal demonstrates the power of 4DMT’s Therapeutic Vector Evolution platform to invent ...

Researchers are shining a light on cancer cells' energy centers -- literally -- to damage these power sources and trigger widespread cancer cell death. In a new study, scientists combined strategies ...

Symptoms of some of the diseases that mimic lung cancer, such as asthma or acid reflux, are common with many conditions. They can include persistent cough, chest pain, shortness of breath, unexplained ...

The company’s pipeline products include LV RP-L102 Fanconi Anemia, Leukocyte Adhesion Deficiency-I, Pyruvate Kinase Deficiency, AAV RP-A501 Danon Disease, AAV RP-A601 PKP2-ACM and AAV BAG3-DCM. Its LV ...

A dual adeno-associated virus (AAV) gene therapy, SB-007 works by delivering the full-length ABCA4 gene, which is intended to reinstate the native ABCA4 protein expression in the retina. Tick here to ...

Adeno-associated viruses (AAV) are powerful instruments in gene therapy. AAV particles comprise a protein capsid that along with the desired genome, containing both is considered a full capsid.

This article explores some of the challenges in developing cell lines for therapeutics, such as cell line stability, and how ...

Lung cancer prognosis tends to be better for people diagnosed in earlier stages of the disease. Once you have received a diagnosis and the type of cancer has been identified, your healthcare provider ...

If you have a lung disease, one treatment option your doctor may suggest is a type of surgery called a lobectomy, which involves removing a portion of your lung called a lobe. Your lungs are made ...