We expect to file the JNDA in mid-2025. These two products are key components of building our rare diseases in Japan could ultimately contribute to the company's overall path to profitability.

In a new study, a team of researchers, including Anneliene Jonker, has published, in Nature Reviews Drug Discovery, the first roadmap for developing genetic therapies for ultra-rare diseases.

The app fiasco cast such a pall over the company’s normally ebullient new product launches that Sonos announced its new flagship Dolby Atmos soundbar — the $999 Sonos Arc Ultra — not with a ...

It’s the supercar you’ve never heard of. Designed by legendary Italian coachbuilder Zagato, powered by an all-American GM small-block V-8, and hand-built in Port Elizabeth, South Africa, the ...

Sweden has quashed plans for 13 offshore wind farms in the Baltic Sea over concerns that they could impede its response to a missile attack. Sweden, which joined NATO earlier this year, shares a ...

It's no secret certain rare coins can be worth a lot of money. Just recently, TikTok user @CoinCollectingWizard sparked huge excitement among collectors after revealing a coin that could be hiding ...

Details remain scarce, but the main reason for pausing plans allegedly comes down to one issue—rare bees. The tech company’s setback, first reported on November 4th by Financial Times ...

AN ULTRA-RARE 50p coin has sold for nearly 300 times its face value. The commemorative Kew Gardens coin, which was minted in 2009, marks 250 years since the botanical gardens opened in 1759.

One special type of pack will aid you in your efforts toward collecting those special cards – the Rare Pack. Here, we’ll explain what this is so you know what to look out for when ripping your ...

A photographer and videographer has captured a rare sight: one particular wild animal of which there are only a few hundred left in the world. Elias Kalliola, 35, from Helsinki, Finland ...